Severe Combined Immunodeficiency - 33 Studies Found
Not yet recruiting |
: Safety and Early Efficacy Study of TBX-1400 in Patients With Severe Combined Immunodeficiencies : Severe Combined Immunodeficiency : 2016-07-26 : Biological: TBX-1400 |
Completed |
: Transplantation of Hematopoietic Cells in Children With Severe Combined Immunodeficiency Syndrome : Severe Combined Immunodeficiency : 2005-09-07 :
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Active, not recruiting |
: Generalized Neonatal Screening of Severe Combined Immunodeficiencies : Severe Combined Immunodeficiency, Atypical : 2014-09-02 : Biological: SCID screening |
Active, not recruiting |
: Clinical Characteristics and Genetic Profiles of Severe Combined Immunodeficiency in China : Severe Combined Immunodeficiency : 2014-09-01 : Genetic: gene sequencing Amplify and identify exons from gene IL-2RG by PCR and agarose gel electrophore |
Completed |
: Stem Cell Gene Therapy to Treat X-Linked Severe Combined Immunodeficiency (XSCID) : Severe Combined Immunodeficiency : 2001-12-17 : Drug: Gene-Transduced Autologous CD34+ Stem Cells |
Active, not recruiting |
: Gene Therapy for X-linked Severe Combined Immunodeficiency : X-linked Severe Combined Immunodeficiency : 2011-06-21 : Other: Gene transfer Single infusion of autologous CD34+ cells transduced with the self-inactivating (SI |
Recruiting |
: Neonatal Screening of Severe Combined Immunodeficiencies :
: 2015-10-27 |
Recruiting |
: Gene Transfer for X-Linked Severe Combined Immunodeficiency in Newly Diagnosed Infants : Severe Combined Immunodeficiency Disease, X-linked : 2012-01-13 :
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Completed |
: Gene Transfer Therapy for Severe Combined Immunodeficieny Disease (SCID) Due to Adenosine Deaminase (ADA) Deficiency: A Natural History Study : Severe Combined Immunodeficiency : 1999-11-03 :
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Recruiting |
: Gene Transfer for Severe Combined Immunodeficiency, X-linked (SCID-X1) Using a Self-inactivating (SIN) Gammaretroviral Vector : Severe Combined Immunodeficiency : 2010-05-21 : Biological: Gene transfer Three procedures: 1) Bone marrow harvest from the patient's posterior iliac cr |